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          <GrantOrContributionPurposeTxt>TESTING OF EXPERIMENTAL THERAPEUTICS IN A ZEBRAFISH MODEL OF FRIEDREICH ATAXIA.</GrantOrContributionPurposeTxt>
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      <AnalysisIncomeProducingActyGrp>
        <FeesContractsFromGovtAgGrp />
        <MembershipDuesAndAssmntGrp />
        <IntOnSavAndTempCashInvstGrp />
        <DividendsAndInterestFromSecDtl>
          <ExclusionCd>14</ExclusionCd>
          <ExclusionAmt>24301</ExclusionAmt>
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        <NetRntlIncmReDebtFincdPropGrp />
        <NetRntlIncmReNotDebtFincdProp />
        <NetRentalIncomePersonalPropGrp />
        <OtherInvestmentIncomeGrp />
        <GainSalesAstOthThanInvntryGrp />
        <NetIncomeLossFromSpecialEvtGrp />
        <GrossProfitLossSlsOfInvntryGrp />
        <SubtotalsIncmProducingActyGrp>
          <ExclusionAmt>24301</ExclusionAmt>
        </SubtotalsIncmProducingActyGrp>
        <TotalIncomeProducingActyAmt>24301</TotalIncomeProducingActyAmt>
      </AnalysisIncomeProducingActyGrp>
      <TrnsfrTransRlnNonchrtblEOGrp>
        <TrnsfrOfCashToNonchrtblEOInd>false</TrnsfrOfCashToNonchrtblEOInd>
        <TrnsfrOtherAssetNonchrtblEOInd>false</TrnsfrOtherAssetNonchrtblEOInd>
        <SalesOrExchangesOfAssetsInd>false</SalesOrExchangesOfAssetsInd>
        <PurchaseOfAssetsNonchrtblEOInd>false</PurchaseOfAssetsNonchrtblEOInd>
        <RentalOfFacilitiesOthAssetsInd>false</RentalOfFacilitiesOthAssetsInd>
        <ReimbursementArrangementsInd>false</ReimbursementArrangementsInd>
        <LoansOrLoanGuaranteesInd>false</LoansOrLoanGuaranteesInd>
        <PerformanceOfServicesEtcInd>false</PerformanceOfServicesEtcInd>
        <SharingOfFacilitiesEtcInd>false</SharingOfFacilitiesEtcInd>
        <RelationshipsNonchrtblEOInd>false</RelationshipsNonchrtblEOInd>
      </TrnsfrTransRlnNonchrtblEOGrp>
    </IRS990PF>
    <IRS990ScheduleB documentId="IRS990ScheduleB">
      <Organization501c3ExemptPFInd>X</Organization501c3ExemptPFInd>
      <GeneralRuleInd>X</GeneralRuleInd>
      <ContributorInformationGrp>
        <ContributorNum>1</ContributorNum>
        <ContributorPersonNm>STIFTUNG AUXILIUM</ContributorPersonNm>
        <ContributorForeignAddress>
          <AddressLine1Txt>Grafenauweg 10</AddressLine1Txt>
          <CityNm>ZUG</CityNm>
          <CountryCd>SZ</CountryCd>
          <ForeignPostalCd>6300</ForeignPostalCd>
        </ContributorForeignAddress>
        <TotalContributionsAmt>5439850</TotalContributionsAmt>
        <PersonContributionInd>X</PersonContributionInd>
      </ContributorInformationGrp>
    </IRS990ScheduleB>
    <DepreciationSchedule documentId="DepreciationSch" />
    <ExpenditureResponsibilityStmt documentId="ExpdturResponbltStmt">
      <ExpenditureResponsibilityGrp>
        <BusinessName>
          <BusinessNameLine1Txt>SEE ATTACHED</BusinessNameLine1Txt>
        </BusinessName>
        <AnyDiversionByGranteeTxt>NO</AnyDiversionByGranteeTxt>
      </ExpenditureResponsibilityGrp>
    </ExpenditureResponsibilityStmt>
    <InvestmentsOtherSchedule2 documentId="InvOtherSch2">
      <InvestmentsOtherGrp>
        <CategoryOrItemTxt>INVESTMENT IN FA212, LLC</CategoryOrItemTxt>
        <ListedAtCostOrFMVCd>FMV</ListedAtCostOrFMVCd>
        <BookValueAmt>4826019</BookValueAmt>
        <EOYFMVAmt>4826019</EOYFMVAmt>
      </InvestmentsOtherGrp>
    </InvestmentsOtherSchedule2>
    <OtherExpensesSchedule documentId="OtherExpensesSch">
      <OtherExpensesScheduleGrp>
        <Desc>DELAWARE FRANCHISE TAX</Desc>
        <RevenueAndExpensesPerBooksAmt>300</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>300</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>NYS FILING FEES</Desc>
        <RevenueAndExpensesPerBooksAmt>250</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>250</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>LICENSES AND PERMITS</Desc>
        <RevenueAndExpensesPerBooksAmt>881</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>881</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>TAX PREPARATION FEES</Desc>
        <RevenueAndExpensesPerBooksAmt>14410</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>14410</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>LEGAL FEES</Desc>
        <RevenueAndExpensesPerBooksAmt>16286</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>16286</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>APP DEVELOPMENT COSTS</Desc>
        <RevenueAndExpensesPerBooksAmt>397541</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>397541</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>INSURANCE EXPENSE</Desc>
        <RevenueAndExpensesPerBooksAmt>17683</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>17683</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>OTHER PROFESSIONAL FEES</Desc>
        <RevenueAndExpensesPerBooksAmt>32814</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>32814</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>BANK CHARGES</Desc>
        <RevenueAndExpensesPerBooksAmt>59</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>59</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
      <OtherExpensesScheduleGrp>
        <Desc>TRAVEL EXPENSE</Desc>
        <RevenueAndExpensesPerBooksAmt>27582</RevenueAndExpensesPerBooksAmt>
        <DisbursementsCharitablePrpsAmt>27582</DisbursementsCharitablePrpsAmt>
      </OtherExpensesScheduleGrp>
    </OtherExpensesSchedule>
    <OtherIncomeSchedule2 documentId="OtherIncomeSch2">
      <OtherIncomeDetail>
        <Desc>ORDINARY LOSS THRU K-1</Desc>
        <RevenueAndExpensesPerBooksAmt>-443960</RevenueAndExpensesPerBooksAmt>
        <NetInvestmentIncomeAmt>-443960</NetInvestmentIncomeAmt>
      </OtherIncomeDetail>
    </OtherIncomeSchedule2>
    <OtherLiabilitiesSchedule documentId="OtherLiabSch">
      <OtherLiabilitiesDetail>
        <Desc>GRANTS DECLARED PAYABLE</Desc>
      </OtherLiabilitiesDetail>
    </OtherLiabilitiesSchedule>
  </ReturnData>
</Return>